Patient and Caregiver Perspectives –
Explore New Developments in Cures, Community, Collaboration and the Care Continuum for Patients and Caregivers
Science Luminaries –
Advancements in Gene Therapy that Are Tearing Down Barriers to Discovery in Rare Disease
Regulatory and Policy Update Address –
Legislative Updates and New Initiatives within the FDA’s Orphan Drug Program
Focus on Funding –
The Impact of Disruptive Investors, Drivers of Value and Funding Models for Success
Technology Spotlight –
Artificial Intelligence (AI) and Advanced Data Analytics — Reshaping Complex Diagnostics and Decision-Making in Rare Disease Drug Development
Venue
Boston Marriott Long Wharf
Organizer
EBD Group
Exhibition has passed
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12—13 June 2019
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Rare Disease Innovation and Partnering Summit 2019 









