Orphan Drugs UK 2017: Discussing strategies for patient engagement, market access and gene therapies to enhance rare disease and orphan drug research
SMi Group is thrilled to present the 7th annual Orphan Drugs and Rare Diseases conference, taking place on 18th and 19th October 2017 in Central London, UK. This year’s theme will be focused towards discussing strategies for patient engagement, market access and gene therapies to enhance rare diseases and orphan drug research.
Aimed at an audience of senior scientists and oncology specialists involved in targeting rare diseases therapies and drug research, Orphan Drugs UK 2017 will provide a perfect platform to discuss pioneering clinical developments and the next generation of clinical trial process. The 7th annual conference will capture expert insight through dedicated focus new therapies for different rare diseases, the importance of orphan drug development and reimbursement and repurposing.
Join us this October for strategic direction from the Rare Disease community and leverage your knowledge with the key requirements and tools for successful patient recruitment and retention through informed guidance delivered by a panel of industry experts.
Featured Speakers:
. Olivier Morand, Clinical Science Program Head, Actelion Pharmaceuticals
. Larissa Kerecuk, Rare Disease Lead, Consultant Paediatric Nephrologist, Birmingham Children’s Hospital
. Oliver Timmis, CEO, AKU Society
. Stuart Hughes, Director, Head of Pharmacology, Vertex
. Christine Lavery, Group Chief Executive, MPS Society
. Olaf Ritzeler, External Innovation Lead, Sanofi
. Stephen Marcus, CEO, Cantex Pharmaceuticals
Exclusive highlights in 2017:
. Learn about new therapies for different rare diseases, and how these can successfully be applied to other diseases with similar attributes
. Hear what opportunities and challenges come with working on rare diseases, as well as the development of the world’s first rare disease centre for children
. Expand your knowledge on patient collaboration and patient centric models with the stream on patient engagement
Speakers: ADB Medical, Chiesi Farmaceutici S.p.A., Sanofi, Summit Therapeutics, Findacure, AKU Society, GlaxoSmithKline, Vertex Pharmaceuticals, MPS Society, Birmingham Children's Hospital, Deutsches Krebsforschungszentrum, Alexion Pharma GmbH, Cantex Pharmaceuticals, Actelion Pharmaceuticals, Action Duchenne, Selecta Biosciences, Cambridge Rare Disease Network (CRDN), Birmingham Children's Hospital
Time: 8:00 am to 5:30 pm
Venue
Holiday Inn Kensington Forum
Organizer
SMi GroupSimilar exhibitions
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Sporting Goods
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Toys, Games, Computer Games
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Trade Fairs, Congresses and Events, Event and Stage Technology
Tube, Wire
Vehicles (Cars, Commercial Vehicles, Motorcycles, Caravans, Parts and Accessories)
Woodworking, Furniture Production
World Expositions
General service trade fairs
Service companies
Other
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Coatings
Packaging, Packaging technology, Printing, Printing technology
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Aerospace Airport Construction
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Books, Prints, Licences, Libraries
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Food, Beverage and Luxury Foodstuff
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National Specialized Exhibitions Abroad
Gifts, Watches Clocks, Jewelry, Crafts, Special Occasion Party Items
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Hotel and Catering, Shop Fittings
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Leather, Leather Goods, Shoes
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Dental Medicine, Dental Technology
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Energy (conventional and renewable)
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Floorings
Food Processing and Packaging Machinery
Food, Beverage and Luxury Foodstuff
Foundry, Metallurgy (Iron, Non-ferrous Metals)
Funerals and Religion
Furniture, Interior Design
Garden and Pet
National Specialized Exhibitions Abroad
Gifts, Watches Clocks, Jewelry, Crafts, Special Occasion Party Items
Hardware, Tools
Hotel and Catering, Shop Fittings
Household Goods and Appliances, Ceramics, Glassware
Industrial Equipment, Maintenance
Information and Communication Technology, Software
Laboratory Technology, Biotechnology
Leather Processing and Shoe Machinery
Leather, Leather Goods, Shoes
Leisure, Hobby, DIY
Lighting, Lighting Technology
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Medical Engineering, Health, Pharmaceuticals, Care
Metalworking, Welding Technology
Mining, Geodesy, Geoinformation
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Nursery Equipment, Childrens Clothing
Office Equipment and Supplies
Oil Gas
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Plastic and Rubber Processing
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Safety, Security, Disaster Control
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Sporting Goods
Subcontracting
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Teaching and Learning Aids, Further and Continuing Education, Business Start-up, Human Resources Development
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Tourism
Toys, Games, Computer Games
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Transport and Traffic
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Floorings
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National Specialized Exhibitions Abroad
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Hotel and Catering, Shop Fittings
Household Goods and Appliances, Ceramics, Glassware
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Other
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Coatings
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Tobacco , tobacco industry , smoking industry
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Arts, Antiques
Boats, Boat Accessories
Books, Prints, Licences, Libraries
Chemical and Petrochemical Industry
City Sanitation, Water Technology, Waste Disposal, Public Services
Clothing, Fashion, Accessories
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Construction Technology, Materials and Equipment, Interior Fittings
Consumer Electronics, Multimedia
Cosmetics, Personal Hygiene, Wellness
Defense Technology
Dental Medicine, Dental Technology
Design Services
Electrical Engineering, Electronics
Energy (conventional and renewable)
Environment and Climate Protection
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Floorings
Food Processing and Packaging Machinery
Food, Beverage and Luxury Foodstuff
Foundry, Metallurgy (Iron, Non-ferrous Metals)
Funerals and Religion
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Garden and Pet
National Specialized Exhibitions Abroad
Gifts, Watches Clocks, Jewelry, Crafts, Special Occasion Party Items
Hardware, Tools
Hotel and Catering, Shop Fittings
Household Goods and Appliances, Ceramics, Glassware
Industrial Equipment, Maintenance
Information and Communication Technology, Software
Laboratory Technology, Biotechnology
Leather Processing and Shoe Machinery
Leather, Leather Goods, Shoes
Leisure, Hobby, DIY
Lighting, Lighting Technology
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Medical Engineering, Health, Pharmaceuticals, Care
Metalworking, Welding Technology
Mining, Geodesy, Geoinformation
Music (Instruments, Licences)
Nursery Equipment, Childrens Clothing
Office Equipment and Supplies
Oil Gas
Ophthalmic Optics
Paper and Printing Industry, Media Production
Photography, Film (Technology, Licences)
Plastic and Rubber Processing
Plumbing, Heating, Air Conditioning, Refrigeration and Ventilation Technology
Safety, Security, Disaster Control
Shipbuilding, Port Machinery, Offshore Engineering
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Subcontracting
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Teaching and Learning Aids, Further and Continuing Education, Business Start-up, Human Resources Development
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Tourism
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Transport and Traffic
Tube, Wire
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World Expositions
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Other
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Clean technology
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Laboratory Technology, Biotechnology
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Nursery Equipment, Childrens Clothing
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